Parent Roundtable: Before and After Gene Therapy

As the revamped 21st Century Cures Act winds its way through the lame duck Congress, I�m reminded of a spellbinding dinner on Sunday night, October 16. It was the eve of the annual "breakthrough summit" for the National Organization for Rare Disorders , and I�d introduced a group of new friends to share their stories of life with a child who has had, or will have, gene therapy.